Weekly Spotlight - 19.12.24

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Latest News

MDA and Coalition to Cure Calpain 3 Fund $300,000 for Limb Girdle Gene Therapy Research

The Muscular Dystrophy Association and the Coalition to Cure Calpain 3 are collaborating to fund a $300,000 research grant focused on developing gene therapy for limb-girdle muscular dystrophy, aiming to advance treatment options for this condition.

MLA Pushes Health Minister for New Drug Access for Duchenne Patients

A local MLA is advocating for the health minister to approve access to a new drug for patients with Duchenne muscular dystrophy, highlighting the potential benefits and urgent need for this treatment to improve the quality of life for those affected.

NICE Approves New Corticosteroid for Duchenne Patients, Offering Alternative Treatment Option.

NICE recommends an alternative corticosteroid, deflazacort, for people with Duchenne muscular dystrophy, offering a new treatment option that may have fewer side effects compared to traditional steroids like prednisolone. This could improve the quality of life for those living with the condition.